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In the spring of 2025 we have begun discussions with a pharmaceutical company who is utilizing lipid nano particles to deliver a good copy of DLG4 mRNA into the body. This treatment path has the potential to reach clinical trials within 18 months. As it's broken down by the body within 48 hours, it is deemed to be a safer approach, and it can be delivered via a port with injections every two days with good distribution throughout the body and shows efficacy as it can pass the blood brain barrier. We are working with a lab on obtaining a DLG4 mouse model to start our efficacy and safety studies simultaneously, begin conversations with the FDA, and identify the treating hospital. We hope to raise at least another $100,00 in the coming year to make this treatment path an option. Please help us support this new technology, which could have a huge impact on the genetic space in the coming years for many diseases. The time is now!
